Program
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- Mesenchymal Stromal Cells
- Commercialization
- Exosomes
- Stem Cell Engineering
- Immuno & Gene Therapies
- Tissue Engineering & Regenerative Medicine
- Plenary
- Concurrent

May 26 - 13:30 EDT
Forecasts demonstrate that approvals-wise, we are looking at 10-20 items being considered per year by 2025. For some time now, we have been lining up to build the research and the knowledge needed for cell and gene therapies to flourish... The questions we can ask now pivot towards how approval should be approached, how reimbursement might look, how patients can get access to therapies, and so on.
Chair
Bruce Levine, PhD
University of Pennsylvania
USA
Peter Marks, MD, PhD
FDA Center for Biologics Evaluation and Research
USA
Arie Belldegrun, MD
Allogene Therapeutics
USA
Matthew Porteus, MD, PhD
Stanford University
USA

May 27 - 08:00 EDT
Description Coming Soon
Presenters:
Co-Chair
Sai-Kiang Lim, PhD
Institute of Molecular & Cell Biology
Singapore
Co-Chair
Maurizio Muraca, MD, PhD
University of Padova
Italy
Stella Kourembanas, MD
Boston Children’s Hospital
USA
Eva Rohde, MD
Paracelsus Medical University
Austria
Andrew Hoffman, DVM, DVSc
University of Pennsylvania
USA

May 27 - 13:30 EDT
We begin with clinical updates exploring the latest data in gene therapy and alternative donor BMT for treating hemoglobinopathies, followed by a moderated debate with leading experts to understand accessibility, cost, endpoints, and outcomes of the currently available therapies for thalassemia and sickle cell disease...
Presenters:
Co-Chair
Jaap Jan Boelens, MD, PhD
Memorial Sloan Kettering
USA
Co-Chair
Sandeep Soni, MD
CRISPR Therapeutics
USA
Alexis Thompson, MD, MPH
Ann & Robert H. Lurie Children's Hospital of Chicago
United States
Suradej Hongeng, MD
Ramathibodi Hospital, Mahidol University
Thailand
Selim Corbacioglu, MD
University Children's Hospital Regensburg
Germany
Matthew Porteus, MD, PhD
Stanford Medicine
USA
Deepa Manwani, MD
The Children's Hospital at Montefiore
USA

May 28 - 08:00 EDT
Description Coming Soon
Presenters:
Co-Chair
Ranieri Cancedda, MD
Università degli Studi di Genova
Italy
Co-Chair
Giuseppe Orlando, MD, PhD
Wake Forest University
USA
Anthony Atala, MD
Wake Forest Institute for Regenerative Medicine
USA
Graziella Pellegrini, PhD
University of Modena and Reggio Emilia
Italy
Rocky Tuan, PhD
Chinese University of Hong Kong
Hong Kong